Articles

  • 3 weeks ago | pharmaceutical-technology.com | Jenna Philpott

    The Advisory Committee on Heritable Disorders in Newborns and Children (ACHDNC) was terminated in April.

  • 3 weeks ago | businessandamerica.com | Jenna Philpott

    After sweeping cuts to US federal health agencies, the elimination of a committee responsible for recommending newborn screening regulations is raising alarms across the healthcare and rare disease communities.  The Advisory Committee on Heritable Disorders in Newborns and Children (ACHDNC), a federally appointed body under the US Health Resources and Services Administration (HRSA), was officially terminated in April.

  • 3 weeks ago | businessandamerica.com | Jenna Philpott

    Eli Lilly is strengthening its position in genetic medicine for hearing loss through a new collaboration with South Korea-based biotech Rznomics.  The agreement, centred on the development of RNA-based gene therapies for sensorineural hearing loss, carries a potential value exceeding $1.3bn in milestone payments. Rznomics disclosed the deal on 15 May, though financial details of the upfront payment were not shared.

  • 3 weeks ago | pharmaceutical-technology.com | Jenna Philpott

    The deal gives Lilly access to the company’s RNA-editing platform to develop therapies for sensorineural hearing loss. The two companies will co-develop precision RNA therapeutics for inherited hearing loss treatment. Credit: Scott Olson/Getty Images News via Getty Images. Eli Lilly is strengthening its position in genetic medicine for hearing loss through a new collaboration with South Korea-based biotech Rznomics.

  • 3 weeks ago | pharmaceutical-technology.com | Jenna Philpott

    The FDA has approved MSD’s Welireg for rare adrenal tumours, and AbbVie’s Emrelis for treating c-Met+ lung cancer patients. The FDA granted approval to both drugs on 14 May. Credit: Waldemarus/iStock via Getty Images. The US Food and Drug Administration (FDA) has approved two oncology drugs: MSD’s Welireg (belzutifan) and AbbVie’s Emrelis (telisotuzumab vedotin-tllv).