Lei Lei Wu

Feb 26, 2025 | endpts.com | Lei Lei Wu

Several small clinical trials have demonstrated that gene therapies have restored hearing in children with a rare form of genetic deafness. In an update at …Sign up to read this article for free. Get free access to a limited number of articles, plus choose newsletters to get straight to your inbox.

Feb 25, 2025 | endpts.com | Lei Lei Wu

To Candel Therapeutics CEO Paul Peter Tak, the biotech’s viral immunotherapy has passed the “bloody obvious test” in pancreatic cancer, and it’s preparing to start …Sign up to read this article for free. Get free access to a limited number of articles, plus choose newsletters to get straight to your inbox.

Feb 24, 2025 | endpts.com | Lei Lei Wu

Entrada Therapeutics announced Monday that the FDA lifted the clinical hold on its Duchenne muscular dystrophy drug, and it plans to start a Phase 1b …Sign up to read this article for free. Get free access to a limited number of articles, plus choose newsletters to get straight to your inbox.

Feb 21, 2025 | endpts.com | Lei Lei Wu

A pair of investors will acquire bluebird bio in a deal worth only $29 million upfront after the gene therapy maker ran out of time …Sign up to read this article for free. Get free access to a limited number of articles, plus choose newsletters to get straight to your inbox.

Feb 20, 2025 | endpts.com | Lei Lei Wu

A mother took the spinal muscular atrophy pill Evrysdi before giving birth to a baby with the devastating genetic disease. The baby, who went on …Sign up to read this article for free. Get free access to a limited number of articles, plus choose newsletters to get straight to your inbox.