Margaret Christy

Dec 13, 2024 | jpedhc.org | Margaret Christy |Beth Fisher

KEY WORDSGene therapysickle cell diseaseadolescenceCRISPRlentiviral vectorGet full text accessLog in, subscribe or purchase for full access. References6. Frangoul, H. ∙ Locatelli, F. ∙ Sharma, A. ... Exagamglogene autotemcel for severe sickle cell diseaseBlood. 2023; 142:10527. GBD 2021 Sickle Cell Disease CollaboratorsGlobal, regional, and national prevalence and mortality burden of sickle cell disease, 2000–2021: A systematic analysis from the Global Burden of Disease Study 2021The Lancet Haematology.